AAV Success Studies | Retinal Dystrophy | Spinal Muscular Atrophy

AAV Success Studies | Retinal Dystrophy | Spinal Muscular Atrophy

Cure One, Cure Many: The Case of Spinal Muscular Atrophy | American Brain FoundationПодробнее

Cure One, Cure Many: The Case of Spinal Muscular Atrophy | American Brain Foundation

Spinal Muscular Atrophy: AVXS-101 Gene Transfer TherapyПодробнее

Spinal Muscular Atrophy: AVXS-101 Gene Transfer Therapy

Spinal Muscular Atrophy 2020: Occupational Therapy Best Practices for Non-SittersПодробнее

Spinal Muscular Atrophy 2020: Occupational Therapy Best Practices for Non-Sitters

Lessons Learned from SMA for DMDПодробнее

Lessons Learned from SMA for DMD

Developing therapies for muscular dystrophy and spinal muscular atrophyПодробнее

Developing therapies for muscular dystrophy and spinal muscular atrophy

MDUK Muscles Matter 2022: Spinal Muscular Atrophy (adult focus)Подробнее

MDUK Muscles Matter 2022: Spinal Muscular Atrophy (adult focus)

2020 Science Writers' Boot Camp: New Treatments for Spinal Muscular Atrophy—Neurodegenetic DiseasesПодробнее

2020 Science Writers' Boot Camp: New Treatments for Spinal Muscular Atrophy—Neurodegenetic Diseases

Gene Therapy Data and Implications of AAV9 AntibodiesПодробнее

Gene Therapy Data and Implications of AAV9 Antibodies

Understanding Spinal Muscular Atrophy (SMA)Подробнее

Understanding Spinal Muscular Atrophy (SMA)

Spinal Muscular Atrophy: Navigating Recent Therapeutic AdvancesПодробнее

Spinal Muscular Atrophy: Navigating Recent Therapeutic Advances

Richard Finkel, AAN 2018 – Spinal muscular atrophy (SMA) is a treatable neurodegenerative diseaseПодробнее

Richard Finkel, AAN 2018 – Spinal muscular atrophy (SMA) is a treatable neurodegenerative disease

Life Saving Spinal Muscular Atrophy (SMA) Treatment | Sam's StoryПодробнее

Life Saving Spinal Muscular Atrophy (SMA) Treatment | Sam's Story

Spinal Muscular Atrophy 2020: Occupational Therapy Best Practices for WalkersПодробнее

Spinal Muscular Atrophy 2020: Occupational Therapy Best Practices for Walkers

Spinal Muscular AtrophyПодробнее

Spinal Muscular Atrophy

Emerging Gene Therapies for Spinal Muscular AtrophyПодробнее

Emerging Gene Therapies for Spinal Muscular Atrophy

Four or More Copies of SMN2 in Patients with Spinal Muscular Atrophy: Treat or Wait?Подробнее

Four or More Copies of SMN2 in Patients with Spinal Muscular Atrophy: Treat or Wait?

Genetic Counseling: Retinal Dystrophy Clinic at UPMC | UPMC On TopicПодробнее

Genetic Counseling: Retinal Dystrophy Clinic at UPMC | UPMC On Topic

Introduction to Spinal Muscular AtrophyПодробнее

Introduction to Spinal Muscular Atrophy

Altering the Natural History of Spinal Muscular AtrophyПодробнее

Altering the Natural History of Spinal Muscular Atrophy